The Fountain-of-Youth Gene: Robert H. Costa's Legacy in the Fight Against Cancer

A Scientific Battle, On and Off the Frontlines

A Scientific Battle, On and Off the Frontlines

In 2002, a molecular geneticist made a discovery so compelling he gave it a poetic nickname: the "fountain-of-youth" gene. By expressing a single gene, FoxM1B, in the cells of old mice, he could make them behave like cells in young, rapidly regenerating mice7 . This scientist was Robert H. Costa, a relentless and innovative leader in cancer research at the University of Illinois at Chicago (UIC)7 .

FoxM1B Discovery

Costa's identification of the FoxM1B gene's role in cellular regeneration earned it the nickname "fountain-of-youth" gene.

Personal Battle

Despite his groundbreaking work against cancer, Costa was diagnosed with stage IV pancreatic cancer in 20063 4 7 .

His pioneering work on this very gene would soon point toward a potential treatment for liver cancer, cementing his status as a star within the scientific community7 .

The FoxM1B Gene: A Key to Regeneration and Cancer

Robert Costa's most significant contributions to science revolved around his identification and study of the Fox family of transcription factors, particularly the gene FoxM1B5 .

What is FoxM1B and why is it crucial?

Master Regulator

FoxM1B controls the expression of genes essential for cell division, DNA replication, and mitosis4 5 .

Regeneration Effect

Introducing FoxM1B into aged mouse livers resulted in regeneration as efficient as in young mice4 7 .

Double-Edged Sword

The same protein that enables regeneration can be hijacked by cancer cells for uncontrolled growth4 5 .

Key Research Reagents in Costa's FoxM1B Studies

Research Reagent/Tool Function in Costa's Research
FoxM1B Transgene A genetically engineered version of the FoxM1B gene used to increase its expression in mouse livers, demonstrating its regenerative capacity4 .
p19ARF Peptide Mimetic A synthetic peptide designed to mimic the tumor suppressor p19ARF, used to inhibit FoxM1B and treat liver cancer in mouse models4 .
Transgenic Mouse Models Genetically modified mice (e.g., TRAMP and LADY) used to study how elevated FoxM1B levels accelerate cancer development5 .

Turning Discovery into Therapy

Costa was not content with merely understanding how cancer forms; he wanted to stop it. His deep knowledge of the FoxM1B system led his lab to design a pioneering therapeutic strategy.

Objective

To determine if a lab-designed peptide mimicking the tumor suppressor p19ARF could inhibit FoxM1B and treat liver cancer in mouse models4 .

Methodology

The researchers created a cell-penetrating ARF peptide inhibitor—essentially, a small protein fragment that could enter cells and block FoxM1B's activity. This peptide was then administered to mice with hepatocellular carcinoma4 .

Results and Analysis

The treatment was a success. The ARF peptide effectively inhibited the progression of hepatocellular carcinoma in the animals4 . This proved that targeting the FoxM1B pathway was a viable and promising strategy for cancer therapy.

1

Gene Targeted

100%

Prevention of Age-Related Proliferation Defects

1

Peptide Inhibitor Developed

Successful

Mouse Model Treatment

A Lasting Scientific Legacy

Robert Costa's untimely death was a profound loss to the scientific community. However, his work continues to inspire and guide researchers today.

Research Impact

His H-index of 87 and nearly 20,000 citations are a testament to the enduring influence of his research5 .

Memorial Lecture

To honor his memory, UIC established the annual Robert H. Costa Memorial Lecture, continuing the spirit of collaboration he championed9 .

Key Publications and Impact

Publication Focus Key Finding Significance
Liver Regeneration & Aging Increased FoxM1B in aged mouse livers prevents age-related proliferation defects4 . Suggested therapeutic potential for improving regenerative healing in aging tissues.
Liver Cancer Development FoxM1B is essential for hepatocellular carcinoma development and is negatively regulated by p19ARF4 . Established FoxM1B as a prime oncogenic target in liver cancer.
Cancer Therapy A cell-penetrating ARF peptide inhibitor of FoxM1B is effective in treating mouse hepatocellular carcinoma4 . Provided a proof-of-concept for a novel cancer treatment strategy.
Transcriptional Networks FoxM1 regulates genes essential for mitotic progression and the SCF ubiquitin ligase5 . Elucidated the fundamental mechanism by which FoxM1 controls cell division.

The Robert H. Costa Memorial Lecture

2024

David Brenner, MD - Liver fibrosis in MASH and the role of LARP69

2022

Vladimir V. Kalinichenko, MD/PhD - Bioengineering and Stem Cell Approaches to Improve Pulmonary Vasculature9

2020

Ralph J. DeBerardinis, MD/PhD - Metabolic phenotypes and cancer progression in humans9

2017

Michael Karin, PhD - New insights into the pathogenesis of NASH and its progression to liver cancer9

2008

Kenneth S. Zaret, PhD - Epigenetic Control by a Pioneer Transcription Factor, FoxA9

The Man Behind the Microscope: A Legacy of Generosity

Beyond his publications and discoveries, Robert Costa was remembered for his exceptional character. Colleagues and friends consistently described him as a generous, supportive, and optimistic individual3 7 .

Infectious Enthusiasm

"When Rob was excited about a finding, you could see it in his eyes, which would light up as he discussed his results"3 .

Unwavering Generosity

Costa was famously generous with his time, expertise, and research reagents, often shipping materials with handwritten notes of encouragement3 .

Courage in Illness

After his diagnosis, he joked about marketing his weight loss as "an alternative to dieting," showing incredible resilience3 7 .

He continued working throughout the summer of 2006, showing incredible resilience and providing a model for how to carry on with purpose and dignity in the most difficult of circumstances7 .

A Legacy of Hope

Robert H. Costa's life and work stand as a powerful reminder that scientific pursuit is not just about data and genes, but about the passion, generosity, and unwavering determination to make a difference. From a "fountain-of-youth" gene to a potential weapon against cancer, his legacy continues to offer hope in the enduring battle against disease.

References